Gene Therapy — Prelims Questions

Which of the following is a common viral vector used in gene therapy that integrates its genetic material into the host cell's genome, providing long-term expression but only in dividing cells?

A 4-year-old child is diagnosed with severe combined immunodeficiency (SCID) due to adenosine deaminase (ADA) deficiency. Which of the following gene therapy approaches would be most appropriate for this condition?

Which of the following statements about germline gene therapy is correct?

Which of the following is NOT a potential challenge or risk associated with gene therapy?

Which of the following statements accurately describes the role of Adeno-Associated Viruses (AAVs) in gene therapy?

Which of the following diseases is a classic example where gene therapy has shown significant promise and is often cited in textbooks as an early success?